Presentations / Publications

TOPPresentations / Publications

Classification Title Presentations / Publications News
Presentation Advanced case report of approval for regenerative medical products 6th Global Quality Assurance Conference, Sendai
2020.2.17-20
Presentation A novel approach to CNS dysfunction of Pompe disease with a fusion protein consisting of anti-transferrin receptor antibody and GAA enzyme 16th Annual WORLDSymposium™ 2020, Florida, USA
2020.2.10-13
Presentation Results from a phase 2 trial of a blood-brain barrier penetrating enzyme (JR-141) in patients with MPS II in Brazil 16th Annual WORLDSymposium™ 2020, Florida, USA
2020.2.10-13
Presentation Therapy for mucopolysaccharidosis II with an intravenous blood-brain barrier-crossing enzyme (JR-141): 26-week results from a phase 3 study in Japan suggesting significant efficacy against central nervous system and systemic symptoms Virus Safety of Pharmaceuticals Symposium, Tokyo
2020.2.8
Presentation Issues in ensuring the quality and safety of allogeneic regenerative medical products Virus Safety of Pharmaceuticals Symposium, Tokyo
2020.2.8
Publication Novel enzyme replacement therapies for neuropathic mucopolysaccharidoses International Journal of Molecular Sciences 2020, 21(2), 400
2020.1.8
Publication Development of therapeutics for Lysosomal Strage Disorders using a Blood-Brain Barrier penetrating technology Official Journal of the Japan Society of Drug Delivery System Vol.34 No.5,
2019. 11
Presentation Cell Therapy Manufacturing: Challenges and Solutions
-Challenges for manufacture of Allogeneic regenerative medicine product-
Regenerative medicine Japan 2019, Yokohama
2019.10.10
Classification Title Presentations / Publications News
Presentation Targeting the Central Nervous System (CNS):
ERT with BBB-penetrating Enzyme vs AAV Gene Therapy in Mouse Model of Mucopolysaccharidosis Type II
The 5th International Forum of Lysosomal Disorders, Tokyo
2019.7.11-13
Presentation Novel enzyme replacement therapies for LSDs: challenges to address neurodegeneration The 5th International Forum of Lysosomal Disorders, Tokyo
2019.7.11-13
Presentation 3rd Generation of electronically-controlled-injectors through the partnership between a Biopharmaceutical and an Electronics company. Prefilled syringe Seminar 2019, Tokyo
2019.5.22
Presentation Establishment and characterization of the human transferrin receptor knock-in mouse The 66th Annual Meeting of the Japanese Association for Laboratory Animal Science, Fukuoka
2019.5.15-17
Presentation The approach for the development of regenerative medicine in JCR pharmaceuticals -effective collaboration with Kobe Biomedical Innovation Cluster- The 18th Congress of the Japanese Society for Regenerative Medicine , Kobe
2019.3.21-23
Presentation Development of therapeutics for rare diseases using a Blood-Brain Barrier penetrating technology 139th Annual Meeting of the Pharmaceutical Society of Japan
2019.3.20-23
Presentation Current situatinon and issues for the development of allogeneic regenerative medicine -through the development of TEMCELL® HS Inj, the first allogeneic mesenchymal stem cell product in Japan- FY2019 Medical Industry Innovation Forum, Tokyo
2019.3.12
Presentation Novel therapeutic approach for treatment of CNS manifestations in patients with Mucopolysaccharidosis 2nd Asia Pacific Lysosomal Conference,New Zealand
2019.2.14-16
Presentation Non-clinical evaluation of a blood-brain barrier -penetrating enzyme for the treatment of Mucopolysaccharidosis I 15th Annual WORLDSymposium™ 2019, Orlando, Florida
2019.2.4-8
Publication Iduronate-2-sulfatase with anti-human transferrin receptor antibody for neuropathic mucopolysaccharidosis II: a phase 1/2 trial Molecular Therapy Volume 27, Issue 2, 6 February 2019, Pages 456-464